Videos

The Promise of Cell and Gene Medicine

Cell and gene medicine can produce life-changing therapies for patients suffering from incurable diseases.

This is an audio-described version of The Promise of Cell & Gene Medicine video. 

[Audio Described]

Cell and Gene Medicine: Your Questions Answered

Host, Matt Might answers your questions about Cell and Gene medicine.

Read the transcript here.

Three young men discuss their hopes for two forms of gene therapy for rare blindness. [Audio Described]Cell and gene medicine can produce life-changing This is an audio-described version of Cell and Gene Medicine: Your Questions Answered.

[Audio Described] 

What is a Clinical Trial?

Clinical Trial Considerations for Patients

A clinical trial helps researchers to determine if a treatment is safe and effective.  Watch the video to learn more.

Questions to ask your healthcare team, and yourself, when considering participation in a clinical trial.

Treating Rare Blindness with Gene Therapy

Three young men discuss their hopes for two forms of gene therapy for rare blindness.

[Closed Captioned]

Three young men discuss their hopes for two forms of gene therapy for rare blindness.

[Audio Described]

Sickle Cell Gene Therapy Trial

Evie James Junior has suffered the pain of sickle cell disease all his life. Recently he participated in a gene therapy clinical trial.

Approved Therapy for Spinal Muscular Atrophy

A young girl’s life was transformed by one of the earliest gene therapies.

A young girl’s life was transformed by one of the earliest gene therapies. [Closed Captioned]

Treating Adult Vision Loss with Gene Therapy

In early phase clinical trial, patients with wet Age-related Macular Degeneration had sight improve.